Growth hormone deficiency type IB caused by cryptic splicing of the GH-1 gene

J Pediatr Endocrinol Metab. 2000 Jan;13(1):21-8. doi: 10.1515/jpem.2000.13.1.21.

Abstract

We have found a novel mutation in intron 4 of the GH-1 gene in a Bedouin kindred with isolated growth hormone deficiency type IB (IGHD IB). RFLP analysis suggested linkage between the GH-1 gene and IGHD. Nested PCR amplification followed by single stranded conformation polymorphism (SSCP) analysis indicated sequence variation between introns 2 and 4. Sequencing showed a G-->C transversion at the fifth base in the splice donor region of intron 4. Affected individuals were homozygous for the mutation, which creates a new Mae III restriction site. Reverse transcription and PCR of GH-1 transcripts in EBV transformed lymphocytes indicated predominance of a species lacking 73 bp of exon 4. Amplification with a bridging primer showed that the same mRNA species is present in lymphocytes from normal individuals. The first 102 amino acids of the predicted protein are identical to wild-type GH, but the next 94 amino acids are completely divergent.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Alternative Splicing*
  • Arabs
  • Base Sequence
  • Child, Preschool
  • Consanguinity
  • Female
  • Human Growth Hormone / deficiency*
  • Human Growth Hormone / genetics*
  • Humans
  • Introns
  • Pedigree
  • Polymorphism, Restriction Fragment Length
  • Polymorphism, Single-Stranded Conformational
  • RNA, Messenger / genetics
  • Reverse Transcriptase Polymerase Chain Reaction
  • Sequence Analysis, DNA

Substances

  • RNA, Messenger
  • Human Growth Hormone