Frontal lobe dementia with abnormal cholesterol metabolism and heterozygous mutation in sterol 27-hydroxylase gene (CYP27)

J Inherit Metab Dis. 2001 Jun;24(3):379-92. doi: 10.1023/a:1010564920930.

Abstract

Of the primary dementing disorders that cause frontotemporal dementia, the best-known is Pick disease. We report on a 44-year-old woman with progressive frontal lobe dementia and spastic paraplegia. Examination revealed increased serum levels of cholestanol with abnormal cholesterol metabolism and a heterozygous mutation of the sterol 27-hydroxylase gene (CYP27). Biochemical findings were compatible with cerebrotendinous xanthomatosis (CTX); however, the clinical manifestations were very dissimilar. To our knowledge, a symptomatic carrier of this mutation among CTX patients has not been reported. We speculate that the present patient has a previously undescribed neurodegenerative disease related to abnormal cholesterol metabolism with this heterozygous mutation.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Bile Acids and Salts / blood
  • Bile Acids and Salts / urine
  • Cholestanetriol 26-Monooxygenase
  • Cholestanol / blood
  • Cholestanols / blood
  • Cholestanols / urine
  • Cholesterol / blood
  • Cholesterol / metabolism*
  • Cytochrome P-450 Enzyme System / genetics*
  • DNA Restriction Enzymes / metabolism
  • DNA, Complementary / chemistry
  • Dementia / diagnosis
  • Dementia / enzymology
  • Dementia / genetics*
  • Female
  • Frontal Lobe*
  • Heterozygote
  • Humans
  • Lipids / blood
  • Lipoproteins / blood
  • Magnetic Resonance Imaging
  • Mutation*
  • Phospholipids / blood
  • Reverse Transcriptase Polymerase Chain Reaction
  • Sequence Analysis, DNA
  • Steroid Hydroxylases / genetics*

Substances

  • Bile Acids and Salts
  • Cholestanols
  • DNA, Complementary
  • Lipids
  • Lipoproteins
  • Phospholipids
  • Cholestanol
  • Cytochrome P-450 Enzyme System
  • Cholesterol
  • Steroid Hydroxylases
  • CYP27A1 protein, human
  • Cholestanetriol 26-Monooxygenase
  • DNA Restriction Enzymes