Episodic ataxia type 2. Three novel truncating mutations and one novel missense mutation in the CACNA1A gene

J Neurol. 2002 Nov;249(11):1515-9. doi: 10.1007/s00415-002-0860-8.

Abstract

We analysed the CACNA1A gene, located on chromosome 19p13, in three unrelated families and one sporadic case with episodic ataxia type 2 (EA-2). In two of the families and the sporadic patient, novel truncating mutations, which disrupt the reading frame and result in a premature stop of the CACNA1A protein, were identified in exons 14, 16 and 26. In the remaining family, a novel missense mutation (H253Y) was found. Of the twenty two EA-2 mutations identified thus far, including those of the present study, seventeen are truncating mutations and five are missense mutations, all resulting in an EA-2 clinical phenotype.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Amino Acid Sequence / genetics
  • Calcium Channels / deficiency*
  • Calcium Channels / genetics*
  • Calcium Channels, P-Type / deficiency*
  • Calcium Channels, P-Type / genetics*
  • Cerebellum / metabolism*
  • Cerebellum / pathology
  • Cerebellum / physiopathology
  • Chromosome Mapping
  • Chromosomes, Human, Pair 19 / genetics
  • DNA Mutational Analysis
  • Exons / genetics
  • Female
  • Genetic Testing
  • Histidine / genetics
  • Humans
  • Male
  • Middle Aged
  • Mutation, Missense / genetics*
  • Pedigree
  • Protein Structure, Tertiary / genetics
  • Spinocerebellar Degenerations / genetics*
  • Spinocerebellar Degenerations / metabolism
  • Spinocerebellar Degenerations / physiopathology
  • Trinucleotide Repeat Expansion / genetics

Substances

  • CACNA1A protein, human
  • Calcium Channels
  • Calcium Channels, P-Type
  • Histidine