The molecular basis of mucopolysaccharidosis type I in two Thai patients

Southeast Asian J Trop Med Public Health. 2005 Sep;36(5):1308-12.

Abstract

Two Thai patients diagnosed with Hurler syndrome (mucopolysaccharidosis type 1, MPS I) were found to have no detectable alpha-iduronidase (E.C. 3.2.1.76) activity in leukocytes, while normal Thai children all had significant activity, with a mean of 135 +/- 30 nmol/mg/18h. One patient was heterozygous for A75T (311G>A) and S633L (1986C>T) mutation, previously reported to cause MPS I, together with 9 other heterozygous polymorphisms also found in normal controls. The other patient had the previously described frameshift mutation 252insert C and a new nonsense mutation E299X (983G>T).

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Base Sequence
  • Child, Preschool
  • DNA Primers
  • Female
  • Humans
  • Mucopolysaccharidosis I / diagnosis
  • Mucopolysaccharidosis I / genetics*
  • Polymorphism, Genetic
  • Sequence Analysis, DNA
  • Thailand

Substances

  • DNA Primers