Deletions of NF1 gene and exons detected by multiplex ligation-dependent probe amplification

J Med Genet. 2007 Dec;44(12):800-8. doi: 10.1136/jmg.2007.053785.

Abstract

To estimate the contribution of single and multi-exon NF1 gene copy-number changes to the NF1 mutation spectrum, we analysed a series of 201 Italian patients with neurofibromatosis type 1 (NF1). Of these, 138 had previously been found, using denaturing high-performance liquid chromatography or protein truncation test, to be heterozygous for intragenic NF1 point mutations/deletions/insertions, and were excluded from this analysis. The remaining 63 patients were analysed using multiplex ligation-dependent probe amplification (MLPA), which allows detection of deletions or duplications encompassing >or=1 NF1 exons, as well as entire gene deletions. MLPA results were validated using real-time quantitative PCR (qPCR) or fluorescent in situ hybridisation. MLPA screening followed by real-time qPCR detected a total of 23 deletions. Of these deletions, six were single exon, eight were multi-exon, and nine were of the entire NF1 gene. In our series, deletions encompassing >or=1 NF1 exons accounted for approximately 7% (14/201) of the NF1 gene mutation spectrum, suggesting that screening for these should now be systematically included in genetic testing of patients with NF1.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Child
  • Child, Preschool
  • Cohort Studies
  • Computer Systems
  • Exons / genetics*
  • Female
  • Gene Deletion*
  • Gene Dosage*
  • Genes, Neurofibromatosis 1*
  • Humans
  • In Situ Hybridization, Fluorescence
  • Infant
  • Italy / epidemiology
  • Male
  • Middle Aged
  • Neurofibromatosis 1 / epidemiology
  • Neurofibromatosis 1 / genetics*
  • Neurofibromatosis 1 / pathology
  • Nucleic Acid Amplification Techniques
  • Phenotype
  • Polymerase Chain Reaction / methods
  • Scoliosis / epidemiology
  • Scoliosis / genetics