Pegfilgrastim in children with severe congenital neutropenia

Pediatr Blood Cancer. 2010 Mar;54(3):465-7. doi: 10.1002/pbc.22350.

Abstract

Two pediatric patients affected by severe congenital neutropenia (SCN) were treated with 100 mcg/L/dose every 9-12 days within a pilot study (Observatory of the Italian Ministry of Health, Eudract Code 2005-003096-20) on the use of pegfilgrastim in patients with chronic neutropenia. Both children increased their absolute neutrophil count, reduced their infectious load, and improved their quality of life. Serum concentrations of G-CSF observed in pegfilgrastim mirrored those seen in filgrastim. These data suggest that pegfilgrastim may be beneficial in SCN patients with an exposure of hematopoietic cells to G-CSF similar to that on filgrastim.

Publication types

  • Case Reports

MeSH terms

  • Child
  • Drug Administration Schedule
  • Female
  • Filgrastim
  • Granulocyte Colony-Stimulating Factor / blood
  • Granulocyte Colony-Stimulating Factor / therapeutic use*
  • Humans
  • Leukocyte Count
  • Male
  • Neutropenia / blood
  • Neutropenia / congenital
  • Neutropenia / drug therapy*
  • Neutrophils / drug effects
  • Neutrophils / pathology
  • Pilot Projects
  • Polyethylene Glycols
  • Recombinant Proteins
  • Treatment Outcome

Substances

  • Recombinant Proteins
  • Granulocyte Colony-Stimulating Factor
  • pegfilgrastim
  • Polyethylene Glycols
  • Filgrastim