Widespread cortical expression of MANF by AAV serotype 7: localization and protection against ischemic brain injury

Exp Neurol. 2010 Sep;225(1):104-13. doi: 10.1016/j.expneurol.2010.05.020. Epub 2010 Jun 2.

Abstract

Mesencephalic astrocyte-derived neurotrophic factor (MANF) is a secreted protein which reduces endoplasmic reticulum (ER) stress and has neurotrophic effects on dopaminergic neurons. Intracortical delivery of recombinant MANF protein protects tissue from ischemic brain injury in vivo. In this study, we examined the protective effect of adeno-associated virus serotype 7 encoding MANF in a rodent model of stroke. An AAV vector containing human MANF cDNA (AAV-MANF) was constructed and verified for expression of MANF protein. AAV-MANF or an AAV control vector was administered into three sites in the cerebral cortex of adult rats. One week after the vector injections, the right middle cerebral artery (MCA) was ligated for 60min. Behavioral monitoring was conducted using body asymmetry analysis, neurological testing, and locomotor activity. Standard immunohistochemical and western blotting procedures were conducted to study MANF expression. Our data showed that AAV-induced MANF expression is redistributed in neurons and glia in cerebral cortex after ischemia. Pretreatment with AAV-MANF reduced the volume of cerebral infarction and facilitated behavioral recovery in stroke rats. In conclusion, our data suggest that intracortical delivery of AAV-MANF increases MANF protein production and reduces ischemic brain injury. Ischemia also caused redistribution of AAV-mediated MANF protein suggesting an injury-induced release.

Publication types

  • Research Support, N.I.H., Intramural

MeSH terms

  • Animals
  • Brain Ischemia / genetics*
  • Brain Ischemia / physiopathology
  • Brain Ischemia / therapy*
  • Cells, Cultured
  • Dependovirus / genetics*
  • Dependovirus / physiology
  • Disease Models, Animal
  • Genetic Therapy / methods*
  • Genetic Vectors / administration & dosage
  • Genetic Vectors / therapeutic use*
  • Humans
  • Infarction, Middle Cerebral Artery / genetics
  • Infarction, Middle Cerebral Artery / physiopathology
  • Infarction, Middle Cerebral Artery / therapy
  • Male
  • Motor Activity / genetics
  • Nerve Growth Factors / biosynthesis
  • Nerve Growth Factors / genetics*
  • Nerve Growth Factors / therapeutic use
  • Proteins / genetics*
  • Proteins / therapeutic use
  • Rats
  • Rats, Sprague-Dawley
  • Recovery of Function / genetics

Substances

  • MANF protein, rat
  • Nerve Growth Factors
  • Proteins