No abstract available
MeSH terms
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Cystic Fibrosis / drug therapy*
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Cystic Fibrosis / genetics*
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Cystic Fibrosis Transmembrane Conductance Regulator / genetics*
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Cystic Fibrosis Transmembrane Conductance Regulator / metabolism*
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Humans
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Molecular Targeted Therapy / trends*
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Mutant Proteins / genetics
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Mutant Proteins / metabolism
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Mutation*
Substances
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CFTR protein, human
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Mutant Proteins
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Cystic Fibrosis Transmembrane Conductance Regulator