Novel HIF2A mutations disrupt oxygen sensing, leading to polycythemia, paragangliomas, and somatostatinomas

Blood. 2013 Mar 28;121(13):2563-6. doi: 10.1182/blood-2012-10-460972. Epub 2013 Jan 29.

Abstract

Hypoxia-inducible factors (HIFs) control the cellular response to hypoxia and, when dysregulated, contribute to tumorigenesis. Previously, we identified 2 gain-of-function somatic mutations in patients presenting with multiple paragangliomas or somatostatinomas, and polycythemia. Here, we report 2 additional unique HIF2A mutations, which disrupt the hydroxylation domain recognized by prolyl hydroxylase domain-2 containing protein, leading to stabilization of HIF-2α and increased expression of hypoxia-related genes.

Publication types

  • Case Reports
  • Research Support, N.I.H., Intramural

MeSH terms

  • Abdominal Neoplasms / genetics
  • Abdominal Neoplasms / metabolism
  • Amino Acid Sequence
  • Base Sequence
  • Basic Helix-Loop-Helix Transcription Factors / chemistry
  • Basic Helix-Loop-Helix Transcription Factors / genetics*
  • Basic Helix-Loop-Helix Transcription Factors / metabolism
  • Child
  • Child, Preschool
  • Female
  • HeLa Cells
  • Humans
  • Models, Molecular
  • Molecular Sequence Data
  • Mutation* / physiology
  • Oxygen / metabolism*
  • Pancreatic Neoplasms / genetics*
  • Pancreatic Neoplasms / metabolism
  • Paraganglioma / genetics*
  • Paraganglioma / metabolism
  • Phylogeny
  • Polycythemia / genetics*
  • Polycythemia / metabolism
  • Somatostatinoma / genetics*
  • Somatostatinoma / metabolism

Substances

  • Basic Helix-Loop-Helix Transcription Factors
  • endothelial PAS domain-containing protein 1
  • Oxygen