Recent progress toward epigenetic therapies: the example of mixed lineage leukemia

Blood. 2013 Jun 13;121(24):4847-53. doi: 10.1182/blood-2013-02-474833. Epub 2013 May 6.

Abstract

The importance of epigenetic gene regulatory mechanisms in normal and cancer development is increasingly evident. Genome-wide analyses have revealed the mutation, deletion, and dysregulated expression of chromatin-modifying enzymes in a number of cancers, including hematologic malignancies. Genome-wide studies of DNA methylation and histone modifications are beginning to reveal the landscape of cancer-specific chromatin patterns. In parallel, recent genetic loss-of-function studies in murine models are demonstrating functional involvement of chromatin-modifying enzymes in malignant cell proliferation and self-renewal. Paradoxically, the same chromatin modifiers can, depending on cancer type, be either hyperactive or inactivated. Increasingly, cross talk between epigenetic pathways is being identified. Leukemias carrying MLL rearrangements are quintessential cancers driven by dysregulated epigenetic mechanisms in which fusion proteins containing N-terminal sequences of MLL require few or perhaps no additional mutations to cause human leukemia. Here, we review how recent progress in the field of epigenetics opens potential mechanism-based therapeutic avenues.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Review

MeSH terms

  • Animals
  • DNA Methylation*
  • DNA, Neoplasm / genetics
  • DNA, Neoplasm / metabolism*
  • Epigenesis, Genetic*
  • Gene Rearrangement / genetics
  • Genome-Wide Association Study
  • Histone-Lysine N-Methyltransferase
  • Humans
  • Leukemia, Biphenotypic, Acute* / genetics
  • Leukemia, Biphenotypic, Acute* / metabolism
  • Leukemia, Biphenotypic, Acute* / pathology
  • Leukemia, Biphenotypic, Acute* / therapy
  • Myeloid-Lymphoid Leukemia Protein / genetics
  • Myeloid-Lymphoid Leukemia Protein / metabolism

Substances

  • DNA, Neoplasm
  • KMT2A protein, human
  • Myeloid-Lymphoid Leukemia Protein
  • Histone-Lysine N-Methyltransferase