Efficacy of long term weekly ACTH therapy for intractable epilepsy

Brain Dev. 2015 Apr;37(4):449-54. doi: 10.1016/j.braindev.2014.07.004. Epub 2014 Aug 20.

Abstract

Background: Adrenocorticotropic hormone (ACTH) therapy is the first-line therapy for infantile spasms, and is effective for many other intractable epilepsies. While spasms may respond to ACTH for weeks, a substantial proportion of patients develop recurrent seizures over a yearly period. To maintain efficacy, we treated two children with intractable epilepsy with weekly ACTH therapy for 1 year and described the changes in clinical seizures, electroencephalograms, developmental assessments and side effects.

Subjects and methods: A girl with infantile spasms due to lissencephaly and a boy with atypical absence seizures were studied. In both cases, seizures were frequent and resistant to antiepileptic drugs; electroencephalograms showed continuous epileptiform activities, and the patients' development was delayed and stagnant prior to ACTH treatment. The initial ACTH therapy (daily 0.015 mg/kg for 2 weeks, 0.015 mg/kg every 2 days for 1 week, 0.0075 mg/kg every 2 days for 1 week), was transiently effective in both cases. The second-round ACTH therapy consisted of the initial ACTH therapy protocol followed by weekly ACTH injections (0.015 mg/kg or 0.0075 mg/kg) for 1 year. Both cases were followed for at least 1 year after therapy.

Results: In both patients, clinical seizures were completely controlled during and 1 year after the second-round AHCH therapy. Continuous epileptiform discharges disappeared, while intermittent interictal epileptiform discharges remained. Both patients showed some developmental gains after achieving seizure control. No serious side effects were recorded.

Conclusion: Further studies are warranted to determine if a long-term weekly ACTH is a safe and effective treatment for intractable epilepsy.

Keywords: ACTH; Atypical absence seizure; Infantile spasms; Intractable epilepsy; LIS1; Lissencephaly.

Publication types

  • Case Reports

MeSH terms

  • Adrenocorticotropic Hormone / administration & dosage*
  • Adrenocorticotropic Hormone / adverse effects
  • Anticonvulsants / administration & dosage*
  • Anticonvulsants / adverse effects
  • Brain / drug effects
  • Brain / pathology
  • Brain / physiopathology
  • Child, Preschool
  • Electroencephalography
  • Epilepsy / drug therapy*
  • Epilepsy / etiology
  • Epilepsy / genetics
  • Epilepsy / physiopathology
  • Female
  • Follow-Up Studies
  • Humans
  • Infant
  • Lissencephaly / complications
  • Lissencephaly / genetics
  • Lissencephaly / physiopathology
  • Magnetic Resonance Imaging
  • Male
  • Recurrence
  • Retreatment / methods
  • Seizures / drug therapy*
  • Seizures / etiology
  • Seizures / genetics
  • Seizures / physiopathology

Substances

  • Anticonvulsants
  • Adrenocorticotropic Hormone