No abstract available
MeSH terms
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Animals
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Antigens, CD34 / genetics
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CRISPR-Cas Systems / genetics
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Gene Editing / methods
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Hematopoietic Stem Cell Transplantation*
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Hematopoietic Stem Cells / metabolism
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Humans
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Iduronidase / genetics*
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Mice
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Mucopolysaccharidosis I / genetics*
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Mucopolysaccharidosis I / pathology
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Mucopolysaccharidosis I / therapy
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Phenotype
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Receptors, CCR5 / genetics*
Substances
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Antigens, CD34
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CCR5 protein, human
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Receptors, CCR5
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IDUA protein, human
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Iduronidase