Netherton syndrome: Temporary response to dupilumab

Pediatr Dermatol. 2020 Nov;37(6):1210-1211. doi: 10.1111/pde.14362. Epub 2020 Sep 19.

Abstract

Netherton syndrome (NS) is an orphan disease characterized by congenital ichthyosis, hair abnormalities, and atopy, with limited treatment options. We achieved temporary improvement only during the initial 6 weeks of treatment with dupilumab, which differs from the sustained improvement observed in 2 other recently published cases. Although the clinical presentation of atopy and increased pre-allergic cytokines in NS patients suggest that dupilumab may be beneficial, larger studies are required.

Keywords: Ichthyosis; atopic eczema; genetic diseases/mechanisms.

MeSH terms

  • Antibodies, Monoclonal, Humanized
  • Hair Diseases*
  • Humans
  • Ichthyosiform Erythroderma, Congenital*
  • Netherton Syndrome* / diagnosis
  • Netherton Syndrome* / drug therapy
  • Netherton Syndrome* / genetics

Substances

  • Antibodies, Monoclonal, Humanized
  • dupilumab