A novel splicing mutation in propionic acidemia associated with a tetranucleotide direct repeat in the PCCB gene

Hum Genet. 1995 Jun;95(6):707-8. doi: 10.1007/BF00209492.

Abstract

Propionic acidemia is an inborn error of organic acid metabolism caused by a deficiency of propionyl Coenzyme A (CoA) carboxylase. cDNAs sequenced from a beta subunit deficient Japanese patient (no. 187) showed an in-frame 57-bp deletion in one allele. Genomic DNA analysis revealed a four-nucleotide deletion of bases 3 to 6 in the 3' intron adjacent to the deleted exon, which disrupted the consensus 5' splice signal and caused exon skipping. This deletion removed one-half of a tetranucleotide direct repeat at the splice junction and presumably resulted from slipped mispairing.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Acyl Coenzyme A / metabolism
  • Base Sequence
  • Carboxy-Lyases / deficiency
  • Carboxy-Lyases / genetics*
  • Female
  • Humans
  • Japan / epidemiology
  • Metabolism, Inborn Errors / epidemiology
  • Metabolism, Inborn Errors / genetics*
  • Methylmalonyl-CoA Decarboxylase
  • Molecular Sequence Data
  • Mutation*
  • Propionates / metabolism
  • RNA Splicing*
  • Repetitive Sequences, Nucleic Acid / genetics*

Substances

  • Acyl Coenzyme A
  • Propionates
  • propionyl-coenzyme A
  • Carboxy-Lyases
  • Methylmalonyl-CoA Decarboxylase
  • propionic acid