Three independent mutations in the same exon of the PCCB gene: differences between Caucasian and Japanese propionic acidaemia

J Inherit Metab Dis. 1993;16(2):353-60. doi: 10.1007/BF00710282.

Abstract

Propionic acidaemia is an inborn error of organic acid metabolism caused by deficiency of propionyl-CoA carboxylase (PCC). Enzyme deficiency can result from mutations in either of the non-identical alpha- and beta-subunits. We have screened genomic DNA from patients with defects in the beta-subunit from two ethnic groups (Caucasians and Japanese) and detected three types of mutations in the same exon of the coding sequence of the beta-subunit: an insertion/deletion that replaces 14 nucleotides with 12 nucleotides of unrelated sequence and eliminates an Msp I site; a 3-bp deletion of a single isoleucine codon immediately proximal to that Msp I site; and a C-->T transition in the same Msp I site. The insertion/deletion was detected only in Caucasian patients in 11 of 34 mutant alleles; the C-->T transition was found only in Japanese patients in 4 of 12 mutant alleles. Following digestion of genomic DNA by Msp I, both of these mutations were detected on Southern blots by the presence of a 2.7-kbp band; they can be distinguished from one another by allele-specific oligonucleotide hybridization following PCR amplification. These results underscore the independent origin of the mutations in the two populations and suggest a key role of this exon in the beta-subunit of PCC.

Publication types

  • Comparative Study
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Amino Acid Metabolism, Inborn Errors / enzymology
  • Amino Acid Metabolism, Inborn Errors / genetics*
  • Asian People / genetics*
  • Base Sequence
  • Blotting, Southern
  • Carboxy-Lyases / deficiency
  • Carboxy-Lyases / genetics*
  • DNA / chemistry
  • DNA / genetics
  • Exons
  • Humans
  • Japan
  • Methylmalonyl-CoA Decarboxylase
  • Molecular Sequence Data
  • Mutation*
  • Polymerase Chain Reaction
  • Propionates / blood*
  • Sequence Analysis, DNA
  • White People / genetics*

Substances

  • Propionates
  • DNA
  • Carboxy-Lyases
  • Methylmalonyl-CoA Decarboxylase