Molecular genetic characterization of an X-linked form of Leigh's syndrome

Ann Neurol. 1993 Jun;33(6):652-5. doi: 10.1002/ana.410330616.

Abstract

We report a patient with necrotizing encephalomyelopathy (Leigh's syndrome) associated with a deficiency of pyruvate dehydrogenase complex activity. The underlying mutation is an A to C transversion in the pyruvate dehydrogenase complex E1 alpha subunit gene. As the E1 alpha subunit is encoded on the X chromosome, this observation confirms that some patients with Leigh's syndrome may potentially exhibit X-linked inheritance.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Amino Acid Sequence
  • Aspartic Acid
  • Base Sequence
  • Brain Stem / pathology
  • Cells, Cultured
  • Cesarean Section
  • Citrate (si)-Synthase / metabolism
  • DNA / genetics
  • DNA / isolation & purification
  • Exons
  • Fibroblasts / pathology
  • Fibroblasts / physiology
  • Gestational Age
  • Humans
  • Infant, Newborn
  • Leigh Disease / genetics*
  • Leigh Disease / pathology
  • Leukocytes / physiology
  • Male
  • Mitochondria, Heart / enzymology
  • Mitochondria, Liver / enzymology
  • Molecular Sequence Data
  • Necrosis
  • Oligodeoxyribonucleotides
  • Point Mutation
  • Pyruvate Dehydrogenase Complex / genetics*
  • Pyruvate Dehydrogenase Complex / metabolism
  • Skin / pathology
  • Skin / physiopathology
  • X Chromosome*

Substances

  • Oligodeoxyribonucleotides
  • Pyruvate Dehydrogenase Complex
  • Aspartic Acid
  • DNA
  • Citrate (si)-Synthase