Etiology
Beck DB,
Bodian DL,
Shah V,
Mirshahi UL,
Kim J,
Ding Y,
Magaziner SJ,
Strande NT,
Cantor A,
Haley JS,
Cook A,
Hill W,
Schwartz AL,
Grayson PC,
Ferrada MA,
Kastner DL,
Carey DJ,
Stewart DR
JAMA
2023 Jan 24;329(4):318-324.
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Li H,
Hu F,
Gale RP,
Sekeres MA,
Liang Y
Nat Rev Dis Primers
2022 Nov 17;8(1):74.
doi: 10.1038/s41572-022-00402-5.
PMID: 36396662
Peffault de Latour R,
Kulasekararaj A,
Iacobelli S,
Terwel SR,
Cook R,
Griffin M,
Halkes CJM,
Recher C,
Barraco F,
Forcade E,
Vallejo JC,
Drexler B,
Mear JB,
Smith AE,
Angelucci E,
Raymakers RAP,
de Groot MR,
Daguindau E,
Nur E,
Barcellini W,
Russell NH,
Terriou L,
Iori AP,
La Rocca U,
Sureda A,
Sánchez-Ortega I,
Xicoy B,
Jarque I,
Cavenagh J,
Sicre de Fontbrune F,
Marotta S,
Munir T,
Tjon JML,
Tavitian S,
Praire A,
Clement L,
Rabian F,
Marano L,
Hill A,
Palmisani E,
Muus P,
Cacace F,
Frieri C,
van Lint MT,
Passweg JR,
Marsh JCW,
Socié G,
Mufti GJ,
Dufour C,
Risitano AM;
Severe Aplastic Anemia Working Party of the European Society for Blood and Marrow Transplantation
N Engl J Med
2022 Jan 6;386(1):11-23.
doi: 10.1056/NEJMoa2109965.
PMID: 34986284
Patnaik MM,
Tefferi A
Am J Hematol
2022 Mar 1;97(3):352-372.
Epub 2022 Jan 27
doi: 10.1002/ajh.26455.
PMID: 34985762
Skokowa J,
Dale DC,
Touw IP,
Zeidler C,
Welte K
Nat Rev Dis Primers
2017 Jun 8;3:17032.
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PMID: 28593997Free PMC Article
Diagnosis
Al-Hakim A,
Savic S
Expert Rev Clin Immunol
2023 Feb;19(2):203-215.
Epub 2022 Dec 26
doi: 10.1080/1744666X.2023.2157262.
PMID: 36537591
Li H,
Hu F,
Gale RP,
Sekeres MA,
Liang Y
Nat Rev Dis Primers
2022 Nov 17;8(1):74.
doi: 10.1038/s41572-022-00402-5.
PMID: 36396662
Patnaik MM,
Tefferi A
Am J Hematol
2022 Mar 1;97(3):352-372.
Epub 2022 Jan 27
doi: 10.1002/ajh.26455.
PMID: 34985762
Garcia-Manero G,
Chien KS,
Montalban-Bravo G
Am J Hematol
2020 Nov;95(11):1399-1420.
doi: 10.1002/ajh.25950.
PMID: 32744763
Brodsky RA
Blood
2014 Oct 30;124(18):2804-11.
Epub 2014 Sep 18
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PMID: 25237200Free PMC Article
Therapy
Li H,
Hu F,
Gale RP,
Sekeres MA,
Liang Y
Nat Rev Dis Primers
2022 Nov 17;8(1):74.
doi: 10.1038/s41572-022-00402-5.
PMID: 36396662
Peffault de Latour R,
Kulasekararaj A,
Iacobelli S,
Terwel SR,
Cook R,
Griffin M,
Halkes CJM,
Recher C,
Barraco F,
Forcade E,
Vallejo JC,
Drexler B,
Mear JB,
Smith AE,
Angelucci E,
Raymakers RAP,
de Groot MR,
Daguindau E,
Nur E,
Barcellini W,
Russell NH,
Terriou L,
Iori AP,
La Rocca U,
Sureda A,
Sánchez-Ortega I,
Xicoy B,
Jarque I,
Cavenagh J,
Sicre de Fontbrune F,
Marotta S,
Munir T,
Tjon JML,
Tavitian S,
Praire A,
Clement L,
Rabian F,
Marano L,
Hill A,
Palmisani E,
Muus P,
Cacace F,
Frieri C,
van Lint MT,
Passweg JR,
Marsh JCW,
Socié G,
Mufti GJ,
Dufour C,
Risitano AM;
Severe Aplastic Anemia Working Party of the European Society for Blood and Marrow Transplantation
N Engl J Med
2022 Jan 6;386(1):11-23.
doi: 10.1056/NEJMoa2109965.
PMID: 34986284
Lee P,
Yim R,
Yung Y,
Chu HT,
Yip PK,
Gill H
Int J Mol Sci
2021 Sep 23;22(19)
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PMID: 34638574Free PMC Article
Skokowa J,
Dale DC,
Touw IP,
Zeidler C,
Welte K
Nat Rev Dis Primers
2017 Jun 8;3:17032.
doi: 10.1038/nrdp.2017.32.
PMID: 28593997Free PMC Article
Hill A,
DeZern AE,
Kinoshita T,
Brodsky RA
Nat Rev Dis Primers
2017 May 18;3:17028.
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Prognosis
Al-Hakim A,
Savic S
Expert Rev Clin Immunol
2023 Feb;19(2):203-215.
Epub 2022 Dec 26
doi: 10.1080/1744666X.2023.2157262.
PMID: 36537591
Koster MJ,
Samec MJ,
Warrington KJ
J Clin Rheumatol
2023 Sep 1;29(6):298-306.
Epub 2022 Oct 17
doi: 10.1097/RHU.0000000000001905.
PMID: 36251488
Li H,
Hu F,
Gale RP,
Sekeres MA,
Liang Y
Nat Rev Dis Primers
2022 Nov 17;8(1):74.
doi: 10.1038/s41572-022-00402-5.
PMID: 36396662
Patnaik MM,
Tefferi A
Am J Hematol
2022 Mar 1;97(3):352-372.
Epub 2022 Jan 27
doi: 10.1002/ajh.26455.
PMID: 34985762
Skokowa J,
Dale DC,
Touw IP,
Zeidler C,
Welte K
Nat Rev Dis Primers
2017 Jun 8;3:17032.
doi: 10.1038/nrdp.2017.32.
PMID: 28593997Free PMC Article
Clinical prediction guides
Beck DB,
Bodian DL,
Shah V,
Mirshahi UL,
Kim J,
Ding Y,
Magaziner SJ,
Strande NT,
Cantor A,
Haley JS,
Cook A,
Hill W,
Schwartz AL,
Grayson PC,
Ferrada MA,
Kastner DL,
Carey DJ,
Stewart DR
JAMA
2023 Jan 24;329(4):318-324.
doi: 10.1001/jama.2022.24836.
PMID: 36692560Free PMC Article
Li H,
Hu F,
Gale RP,
Sekeres MA,
Liang Y
Nat Rev Dis Primers
2022 Nov 17;8(1):74.
doi: 10.1038/s41572-022-00402-5.
PMID: 36396662
Sahoo SS,
Pastor VB,
Goodings C,
Voss RK,
Kozyra EJ,
Szvetnik A,
Noellke P,
Dworzak M,
Starý J,
Locatelli F,
Masetti R,
Schmugge M,
De Moerloose B,
Catala A,
Kállay K,
Turkiewicz D,
Hasle H,
Buechner J,
Jahnukainen K,
Ussowicz M,
Polychronopoulou S,
Smith OP,
Fabri O,
Barzilai S,
de Haas V,
Baumann I,
Schwarz-Furlan S;
European Working Group of MDS in Children (EWOG-MDS),
Niewisch MR,
Sauer MG,
Burkhardt B,
Lang P,
Bader P,
Beier R,
Müller I,
Albert MH,
Meisel R,
Schulz A,
Cario G,
Panda PK,
Wehrle J,
Hirabayashi S,
Derecka M,
Durruthy-Durruthy R,
Göhring G,
Yoshimi-Noellke A,
Ku M,
Lebrecht D,
Erlacher M,
Flotho C,
Strahm B,
Niemeyer CM,
Wlodarski MW
Nat Med
2021 Oct;27(10):1806-1817.
Epub 2021 Oct 7
doi: 10.1038/s41591-021-01511-6.
PMID: 34621053Free PMC Article
Garcia-Manero G,
Chien KS,
Montalban-Bravo G
Am J Hematol
2020 Nov;95(11):1399-1420.
doi: 10.1002/ajh.25950.
PMID: 32744763
Sood R,
Kamikubo Y,
Liu P
Blood
2017 Apr 13;129(15):2070-2082.
Epub 2017 Feb 8
doi: 10.1182/blood-2016-10-687830.
PMID: 28179279Free PMC Article