Etiology
Del Bufalo F,
De Angelis B,
Caruana I,
Del Baldo G,
De Ioris MA,
Serra A,
Mastronuzzi A,
Cefalo MG,
Pagliara D,
Amicucci M,
Li Pira G,
Leone G,
Bertaina V,
Sinibaldi M,
Di Cecca S,
Guercio M,
Abbaszadeh Z,
Iaffaldano L,
Gunetti M,
Iacovelli S,
Bugianesi R,
Macchia S,
Algeri M,
Merli P,
Galaverna F,
Abbas R,
Garganese MC,
Villani MF,
Colafati GS,
Bonetti F,
Rabusin M,
Perruccio K,
Folsi V,
Quintarelli C,
Locatelli F;
Precision Medicine Team–IRCCS Ospedale Pediatrico Bambino Gesù
N Engl J Med
2023 Apr 6;388(14):1284-1295.
doi: 10.1056/NEJMoa2210859.
PMID: 37018492
Qiu B,
Matthay KK
Nat Rev Clin Oncol
2022 Aug;19(8):515-533.
Epub 2022 May 25
doi: 10.1038/s41571-022-00643-z.
PMID: 35614230
DuBois SG,
Macy ME,
Henderson TO
Am Soc Clin Oncol Educ Book
2022 Apr;42:1-13.
doi: 10.1200/EDBK_349783.
PMID: 35522915
Ponzoni M,
Bachetti T,
Corrias MV,
Brignole C,
Pastorino F,
Calarco E,
Bensa V,
Giusto E,
Ceccherini I,
Perri P
J Exp Clin Cancer Res
2022 Mar 11;41(1):92.
doi: 10.1186/s13046-022-02281-w.
PMID: 35277192Free PMC Article
Juraschka K,
Taylor MD
J Neurosurg Pediatr
2019 Oct 1;24(4):353-363.
doi: 10.3171/2019.5.PEDS18381.
PMID: 31574483
Diagnosis
Goldsmith KC,
Park JR,
Kayser K,
Malvar J,
Chi YY,
Groshen SG,
Villablanca JG,
Krytska K,
Lai LM,
Acharya PT,
Goodarzian F,
Pawel B,
Shimada H,
Ghazarian S,
States L,
Marshall L,
Chesler L,
Granger M,
Desai AV,
Mody R,
Morgenstern DA,
Shusterman S,
Macy ME,
Pinto N,
Schleiermacher G,
Vo K,
Thurm HC,
Chen J,
Liyanage M,
Peltz G,
Matthay KK,
Berko ER,
Maris JM,
Marachelian A,
Mossé YP
Nat Med
2023 May;29(5):1092-1102.
Epub 2023 Apr 3
doi: 10.1038/s41591-023-02297-5.
PMID: 37012551Free PMC Article
DuBois SG,
Macy ME,
Henderson TO
Am Soc Clin Oncol Educ Book
2022 Apr;42:1-13.
doi: 10.1200/EDBK_349783.
PMID: 35522915
Suk Y,
Gwynne WD,
Burns I,
Venugopal C,
Singh SK
Methods Mol Biol
2022;2423:1-12.
doi: 10.1007/978-1-0716-1952-0_1.
PMID: 34978683
Rafael MS,
Cohen-Gogo S,
Irwin MS,
Vali R,
Shammas A,
Morgenstern DA
PET Clin
2021 Jul;16(3):419-427.
doi: 10.1016/j.cpet.2021.03.006.
PMID: 34053585
Schengrund CL
Int J Mol Sci
2020 Jul 27;21(15)
doi: 10.3390/ijms21155313.
PMID: 32726962Free PMC Article
Therapy
Del Bufalo F,
De Angelis B,
Caruana I,
Del Baldo G,
De Ioris MA,
Serra A,
Mastronuzzi A,
Cefalo MG,
Pagliara D,
Amicucci M,
Li Pira G,
Leone G,
Bertaina V,
Sinibaldi M,
Di Cecca S,
Guercio M,
Abbaszadeh Z,
Iaffaldano L,
Gunetti M,
Iacovelli S,
Bugianesi R,
Macchia S,
Algeri M,
Merli P,
Galaverna F,
Abbas R,
Garganese MC,
Villani MF,
Colafati GS,
Bonetti F,
Rabusin M,
Perruccio K,
Folsi V,
Quintarelli C,
Locatelli F;
Precision Medicine Team–IRCCS Ospedale Pediatrico Bambino Gesù
N Engl J Med
2023 Apr 6;388(14):1284-1295.
doi: 10.1056/NEJMoa2210859.
PMID: 37018492
Goldsmith KC,
Park JR,
Kayser K,
Malvar J,
Chi YY,
Groshen SG,
Villablanca JG,
Krytska K,
Lai LM,
Acharya PT,
Goodarzian F,
Pawel B,
Shimada H,
Ghazarian S,
States L,
Marshall L,
Chesler L,
Granger M,
Desai AV,
Mody R,
Morgenstern DA,
Shusterman S,
Macy ME,
Pinto N,
Schleiermacher G,
Vo K,
Thurm HC,
Chen J,
Liyanage M,
Peltz G,
Matthay KK,
Berko ER,
Maris JM,
Marachelian A,
Mossé YP
Nat Med
2023 May;29(5):1092-1102.
Epub 2023 Apr 3
doi: 10.1038/s41591-023-02297-5.
PMID: 37012551Free PMC Article
Qiu B,
Matthay KK
Nat Rev Clin Oncol
2022 Aug;19(8):515-533.
Epub 2022 May 25
doi: 10.1038/s41571-022-00643-z.
PMID: 35614230
DuBois SG,
Macy ME,
Henderson TO
Am Soc Clin Oncol Educ Book
2022 Apr;42:1-13.
doi: 10.1200/EDBK_349783.
PMID: 35522915
Heczey A,
Courtney AN,
Montalbano A,
Robinson S,
Liu K,
Li M,
Ghatwai N,
Dakhova O,
Liu B,
Raveh-Sadka T,
Chauvin-Fleurence CN,
Xu X,
Ngai H,
Di Pierro EJ,
Savoldo B,
Dotti G,
Metelitsa LS
Nat Med
2020 Nov;26(11):1686-1690.
Epub 2020 Oct 12
doi: 10.1038/s41591-020-1074-2.
PMID: 33046868
Prognosis
Qiu B,
Matthay KK
Nat Rev Clin Oncol
2022 Aug;19(8):515-533.
Epub 2022 May 25
doi: 10.1038/s41571-022-00643-z.
PMID: 35614230
DuBois SG,
Macy ME,
Henderson TO
Am Soc Clin Oncol Educ Book
2022 Apr;42:1-13.
doi: 10.1200/EDBK_349783.
PMID: 35522915
Suk Y,
Gwynne WD,
Burns I,
Venugopal C,
Singh SK
Methods Mol Biol
2022;2423:1-12.
doi: 10.1007/978-1-0716-1952-0_1.
PMID: 34978683
Mody R,
Yu AL,
Naranjo A,
Zhang FF,
London WB,
Shulkin BL,
Parisi MT,
Servaes SE,
Diccianni MB,
Hank JA,
Felder M,
Birstler J,
Sondel PM,
Asgharzadeh S,
Glade-Bender J,
Katzenstein H,
Maris JM,
Park JR,
Bagatell R
J Clin Oncol
2020 Jul 1;38(19):2160-2169.
Epub 2020 Apr 28
doi: 10.1200/JCO.20.00203.
PMID: 32343642Free PMC Article
Juraschka K,
Taylor MD
J Neurosurg Pediatr
2019 Oct 1;24(4):353-363.
doi: 10.3171/2019.5.PEDS18381.
PMID: 31574483
Clinical prediction guides
Del Bufalo F,
De Angelis B,
Caruana I,
Del Baldo G,
De Ioris MA,
Serra A,
Mastronuzzi A,
Cefalo MG,
Pagliara D,
Amicucci M,
Li Pira G,
Leone G,
Bertaina V,
Sinibaldi M,
Di Cecca S,
Guercio M,
Abbaszadeh Z,
Iaffaldano L,
Gunetti M,
Iacovelli S,
Bugianesi R,
Macchia S,
Algeri M,
Merli P,
Galaverna F,
Abbas R,
Garganese MC,
Villani MF,
Colafati GS,
Bonetti F,
Rabusin M,
Perruccio K,
Folsi V,
Quintarelli C,
Locatelli F;
Precision Medicine Team–IRCCS Ospedale Pediatrico Bambino Gesù
N Engl J Med
2023 Apr 6;388(14):1284-1295.
doi: 10.1056/NEJMoa2210859.
PMID: 37018492
Su Y,
Luo B,
Lu Y,
Wang D,
Yan J,
Zheng J,
Xiao J,
Wang Y,
Xue Z,
Yin J,
Chen P,
Li L,
Zhao Q
Clin Cancer Res
2022 Feb 15;28(4):793-809.
doi: 10.1158/1078-0432.CCR-21-2241.
PMID: 34844980Free PMC Article
Levy AS,
Krailo M,
Chi S,
Villaluna D,
Springer L,
Williams-Hughes C,
Fouladi M,
Gajjar A
Pediatr Blood Cancer
2021 Aug;68(8):e29031.
Epub 2021 Apr 12
doi: 10.1002/pbc.29031.
PMID: 33844469Free PMC Article
Heczey A,
Courtney AN,
Montalbano A,
Robinson S,
Liu K,
Li M,
Ghatwai N,
Dakhova O,
Liu B,
Raveh-Sadka T,
Chauvin-Fleurence CN,
Xu X,
Ngai H,
Di Pierro EJ,
Savoldo B,
Dotti G,
Metelitsa LS
Nat Med
2020 Nov;26(11):1686-1690.
Epub 2020 Oct 12
doi: 10.1038/s41591-020-1074-2.
PMID: 33046868
Mody R,
Yu AL,
Naranjo A,
Zhang FF,
London WB,
Shulkin BL,
Parisi MT,
Servaes SE,
Diccianni MB,
Hank JA,
Felder M,
Birstler J,
Sondel PM,
Asgharzadeh S,
Glade-Bender J,
Katzenstein H,
Maris JM,
Park JR,
Bagatell R
J Clin Oncol
2020 Jul 1;38(19):2160-2169.
Epub 2020 Apr 28
doi: 10.1200/JCO.20.00203.
PMID: 32343642Free PMC Article