Etiology
Peffault de Latour R,
Kulasekararaj A,
Iacobelli S,
Terwel SR,
Cook R,
Griffin M,
Halkes CJM,
Recher C,
Barraco F,
Forcade E,
Vallejo JC,
Drexler B,
Mear JB,
Smith AE,
Angelucci E,
Raymakers RAP,
de Groot MR,
Daguindau E,
Nur E,
Barcellini W,
Russell NH,
Terriou L,
Iori AP,
La Rocca U,
Sureda A,
Sánchez-Ortega I,
Xicoy B,
Jarque I,
Cavenagh J,
Sicre de Fontbrune F,
Marotta S,
Munir T,
Tjon JML,
Tavitian S,
Praire A,
Clement L,
Rabian F,
Marano L,
Hill A,
Palmisani E,
Muus P,
Cacace F,
Frieri C,
van Lint MT,
Passweg JR,
Marsh JCW,
Socié G,
Mufti GJ,
Dufour C,
Risitano AM;
Severe Aplastic Anemia Working Party of the European Society for Blood and Marrow Transplantation
N Engl J Med
2022 Jan 6;386(1):11-23.
doi: 10.1056/NEJMoa2109965.
PMID: 34986284
Patel BA,
Groarke EM,
Lotter J,
Shalhoub R,
Gutierrez-Rodrigues F,
Rios O,
Quinones Raffo D,
Wu CO,
Young NS
Blood
2022 Jan 6;139(1):34-43.
doi: 10.1182/blood.2021012130.
PMID: 34525188Free PMC Article
Shimano KA,
Narla A,
Rose MJ,
Gloude NJ,
Allen SW,
Bergstrom K,
Broglie L,
Carella BA,
Castillo P,
de Jong JLO,
Dror Y,
Geddis AE,
Huang JN,
Lau BW,
McGuinn C,
Nakano TA,
Overholt K,
Rothman JA,
Sharathkumar A,
Shereck E,
Vlachos A,
Olson TS,
Bertuch AA,
Wlodarski MW,
Shimamura A,
Boklan J
Am J Hematol
2021 Nov 1;96(11):1491-1504.
Epub 2021 Aug 20
doi: 10.1002/ajh.26310.
PMID: 34342889
Georges GE,
Doney K,
Storb R
Blood Adv
2018 Aug 14;2(15):2020-2028.
doi: 10.1182/bloodadvances.2018021162.
PMID: 30108110Free PMC Article
Townsley DM,
Scheinberg P,
Winkler T,
Desmond R,
Dumitriu B,
Rios O,
Weinstein B,
Valdez J,
Lotter J,
Feng X,
Desierto M,
Leuva H,
Bevans M,
Wu C,
Larochelle A,
Calvo KR,
Dunbar CE,
Young NS
N Engl J Med
2017 Apr 20;376(16):1540-1550.
doi: 10.1056/NEJMoa1613878.
PMID: 28423296Free PMC Article
Diagnosis
Shimano KA,
Narla A,
Rose MJ,
Gloude NJ,
Allen SW,
Bergstrom K,
Broglie L,
Carella BA,
Castillo P,
de Jong JLO,
Dror Y,
Geddis AE,
Huang JN,
Lau BW,
McGuinn C,
Nakano TA,
Overholt K,
Rothman JA,
Sharathkumar A,
Shereck E,
Vlachos A,
Olson TS,
Bertuch AA,
Wlodarski MW,
Shimamura A,
Boklan J
Am J Hematol
2021 Nov 1;96(11):1491-1504.
Epub 2021 Aug 20
doi: 10.1002/ajh.26310.
PMID: 34342889
Georges GE,
Doney K,
Storb R
Blood Adv
2018 Aug 14;2(15):2020-2028.
doi: 10.1182/bloodadvances.2018021162.
PMID: 30108110Free PMC Article
Peslak SA,
Olson T,
Babushok DV
Curr Treat Options Oncol
2017 Nov 16;18(12):70.
doi: 10.1007/s11864-017-0511-z.
PMID: 29143887Free PMC Article
Bacigalupo A
Blood
2017 Mar 16;129(11):1428-1436.
Epub 2017 Jan 17
doi: 10.1182/blood-2016-08-693481.
PMID: 28096088
Hartung HD,
Olson TS,
Bessler M
Pediatr Clin North Am
2013 Dec;60(6):1311-36.
Epub 2013 Oct 16
doi: 10.1016/j.pcl.2013.08.011.
PMID: 24237973Free PMC Article
Therapy
Peffault de Latour R,
Kulasekararaj A,
Iacobelli S,
Terwel SR,
Cook R,
Griffin M,
Halkes CJM,
Recher C,
Barraco F,
Forcade E,
Vallejo JC,
Drexler B,
Mear JB,
Smith AE,
Angelucci E,
Raymakers RAP,
de Groot MR,
Daguindau E,
Nur E,
Barcellini W,
Russell NH,
Terriou L,
Iori AP,
La Rocca U,
Sureda A,
Sánchez-Ortega I,
Xicoy B,
Jarque I,
Cavenagh J,
Sicre de Fontbrune F,
Marotta S,
Munir T,
Tjon JML,
Tavitian S,
Praire A,
Clement L,
Rabian F,
Marano L,
Hill A,
Palmisani E,
Muus P,
Cacace F,
Frieri C,
van Lint MT,
Passweg JR,
Marsh JCW,
Socié G,
Mufti GJ,
Dufour C,
Risitano AM;
Severe Aplastic Anemia Working Party of the European Society for Blood and Marrow Transplantation
N Engl J Med
2022 Jan 6;386(1):11-23.
doi: 10.1056/NEJMoa2109965.
PMID: 34986284
Patel BA,
Groarke EM,
Lotter J,
Shalhoub R,
Gutierrez-Rodrigues F,
Rios O,
Quinones Raffo D,
Wu CO,
Young NS
Blood
2022 Jan 6;139(1):34-43.
doi: 10.1182/blood.2021012130.
PMID: 34525188Free PMC Article
Bussel JB,
Soff G,
Balduzzi A,
Cooper N,
Lawrence T,
Semple JW
Drug Des Devel Ther
2021;15:2243-2268.
Epub 2021 May 26
doi: 10.2147/DDDT.S299591.
PMID: 34079225Free PMC Article
Ghanima W,
Cooper N,
Rodeghiero F,
Godeau B,
Bussel JB
Haematologica
2019 Jun;104(6):1112-1123.
Epub 2019 May 9
doi: 10.3324/haematol.2018.212845.
PMID: 31073079Free PMC Article
Townsley DM,
Scheinberg P,
Winkler T,
Desmond R,
Dumitriu B,
Rios O,
Weinstein B,
Valdez J,
Lotter J,
Feng X,
Desierto M,
Leuva H,
Bevans M,
Wu C,
Larochelle A,
Calvo KR,
Dunbar CE,
Young NS
N Engl J Med
2017 Apr 20;376(16):1540-1550.
doi: 10.1056/NEJMoa1613878.
PMID: 28423296Free PMC Article
Prognosis
Zhang Y,
He Y,
Wang S,
Sun J,
Jia J,
Gong Y,
He G,
Li J
Front Immunol
2023;14:1197982.
Epub 2023 Jul 11
doi: 10.3389/fimmu.2023.1197982.
PMID: 37497227Free PMC Article
Kulasekararaj AG,
Hill A,
Rottinghaus ST,
Langemeijer S,
Wells R,
Gonzalez-Fernandez FA,
Gaya A,
Lee JW,
Gutierrez EO,
Piatek CI,
Szer J,
Risitano A,
Nakao S,
Bachman E,
Shafner L,
Damokosh AI,
Ortiz S,
Röth A,
Peffault de Latour R
Blood
2019 Feb 7;133(6):540-549.
Epub 2018 Dec 3
doi: 10.1182/blood-2018-09-876805.
PMID: 30510079Free PMC Article
Bacigalupo A
Blood
2017 Mar 16;129(11):1428-1436.
Epub 2017 Jan 17
doi: 10.1182/blood-2016-08-693481.
PMID: 28096088
Hartung HD,
Olson TS,
Bessler M
Pediatr Clin North Am
2013 Dec;60(6):1311-36.
Epub 2013 Oct 16
doi: 10.1016/j.pcl.2013.08.011.
PMID: 24237973Free PMC Article
Scheinberg P,
Nunez O,
Weinstein B,
Scheinberg P,
Biancotto A,
Wu CO,
Young NS
N Engl J Med
2011 Aug 4;365(5):430-8.
doi: 10.1056/NEJMoa1103975.
PMID: 21812672Free PMC Article
Clinical prediction guides
Risitano AM,
Frieri C,
Urciuoli E,
Marano L
Immunol Rev
2023 Jan;313(1):262-278.
Epub 2022 Sep 15
doi: 10.1111/imr.13137.
PMID: 36110036Free PMC Article
McReynolds LJ,
Rafati M,
Wang Y,
Ballew BJ,
Kim J,
Williams VV,
Zhou W,
Hendricks RM,
Dagnall C,
Freedman ND,
Carter B,
Strollo S,
Hicks B,
Zhu B,
Jones K,
Paczesny S,
Marsh SGE,
Spellman SR,
He M,
Wang T,
Lee SJ,
Savage SA,
Gadalla SM
Blood
2022 Aug 25;140(8):909-921.
doi: 10.1182/blood.2022016508.
PMID: 35776903Free PMC Article
Patel BA,
Groarke EM,
Lotter J,
Shalhoub R,
Gutierrez-Rodrigues F,
Rios O,
Quinones Raffo D,
Wu CO,
Young NS
Blood
2022 Jan 6;139(1):34-43.
doi: 10.1182/blood.2021012130.
PMID: 34525188Free PMC Article
Locatelli F,
Strahm B
Blood
2018 Mar 29;131(13):1406-1414.
Epub 2018 Feb 8
doi: 10.1182/blood-2017-09-765214.
PMID: 29438960
Bacigalupo A
Blood
2017 Mar 16;129(11):1428-1436.
Epub 2017 Jan 17
doi: 10.1182/blood-2016-08-693481.
PMID: 28096088